Rare Disease Discussions
Rare Disease Discussions
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Investigational Drug Provides Improved Quality of Life for PNH Patients
7 minutes Posted Apr 15, 2021 at 8:07 pm.
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Cedric Francois, MD, PhD, Co-Founder & CEO of Apellis Pharmaceuticals, discusses the results of the PEGASUS study evaluating the efficacy and safety of pegcetacoplan in patients with paroxysmal nocturnal hemoglobinuria (PNH).