MyFSHD
MyFSHD
Peter L Jones, PhD
Antisense, gene therapy, and stem cell news, and the Blues Brothers
1 hour 26 minutes Posted Dec 15, 2022 at 3:27 am.
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Show notes

"I want four fried chickens and a Coke".  Dr. Charis Himeda joins us as we discuss some encouraging recent data from Sarepta for one of their DMD gene therapy trials and from Avidity for their myotonic dystrophy phase I/II trial and how it all potentially impacts FSHD.  In addition, we revisit the potential (or lack there of) for placental or umbilical cord derived stem cell therapy for FSHD.